FDA approves Soliris for rare pediatric blood disorder The U.S.
FDA approves Soliris for rare pediatric blood disorder
The U.S. Food and Drug Administration today approved Soliris (eculizumab) to treat patients with atypical Hemolytic Uremic Syndrome (aHUS), a rare and chronic blood disease that can lead to kidney (renal) failure and is also associated with increased risk of death and stroke.